Cellular defect found in inherited and sporadic ALS
August 10, 2021
Cellular defect found in inherited and sporadic ALS
At a Glance
- In lab-grown neurons derived from people with inherited or sporadic ALS, buildup of a protein called CHMP7 in the nucleus led to cellular damage.
- Using a drug to block this buildup prevented damage, suggesting a strategy to treat both inherited and sporadic ALS.